https://www.selleckchem.com/pr....oducts/gsk1838705a.h
Evidence to guide treatment of pediatric medium-chain acyl-coenzyme A dehydrogenase (MCAD) deficiency and phenylketonuria (PKU) is fragmented because of large variability in outcome selection and measurement. Our goal was to develop core outcome sets (COSs) for these diseases to facilitate meaningful future evidence generation and enhance the capacity to compare and synthesize findings across studies. Parents and/or caregivers, health professionals, and health policy advisors completed a Delphi survey and participated in a consensus
Like
Comment
Share
